scholarly journals Therapeutic benefit of lentiviral-mediated neonatal intracerebral gene therapy in a mouse model of globoid cell leukodystrophy

2014 ◽  
Vol 23 (12) ◽  
pp. 3250-3268 ◽  
Author(s):  
A. Lattanzi ◽  
C. Salvagno ◽  
C. Maderna ◽  
F. Benedicenti ◽  
F. Morena ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Mouse Model ◽  
Therapeutic Benefit ◽  
Globoid Cell Leukodystrophy ◽  
Globoid Cell

scholarly journals Neural Stem Cell Gene Therapy Ameliorates Pathology and Function in a Mouse Model of Globoid Cell Leukodystrophy

Stem Cells ◽  
2011 ◽  
Vol 29 (10) ◽  
pp. 1559-1571 ◽  
Author(s):  
Margherita Neri ◽  
Alessandra Ricca ◽  
Ilaria di Girolamo ◽  
Beatriz Alcala'-Franco ◽  
Chiara Cavazzin ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Stem Cell ◽  
Mouse Model ◽  
Neural Stem Cell ◽  
Globoid Cell Leukodystrophy ◽  
And Function ◽  
Cell Gene ◽  
Stem Cell Gene ◽  
Stem Cell Gene Therapy ◽  
Globoid Cell

Identification of Hematopoietic Stem Cell-Specific miRNAs Enables Gene Therapy of Globoid Cell Leukodystrophy

2010 ◽  
Vol 2 (58) ◽  
pp. 58ra84-58ra84 ◽  
Author(s):  
B. Gentner ◽  
I. Visigalli ◽  
H. Hiramatsu ◽  
E. Lechman ◽  
S. Ungari ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Stem Cell ◽  
Hematopoietic Stem Cell ◽  
Globoid Cell Leukodystrophy ◽  
Hematopoietic Stem ◽  
Globoid Cell

scholarly journals 56. Intracerebroventricular and Intravenous AAV Gene Therapy in Canine Globoid Cell Leukodystrophy

2016 ◽  
Vol 24 ◽  
pp. S24-S25
Author(s):  
Allison M. Bradbury ◽  
Mohammad Rafi ◽  
Gary P. Swain ◽  
Jessica H. Bagel ◽  
Maria Prociuk ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Globoid Cell Leukodystrophy ◽  
Globoid Cell

Single‐dose intracerebroventricular administration of galactocerebrosidase improves survival in a mouse model of globoid cell leukodystrophy

2007 ◽  
Vol 21 (10) ◽  
pp. 2520-2527 ◽  
Author(s):  
Wing C. Lee ◽  
Yuen K. Tsoi ◽  
Frederick J. Troendle ◽  
Michael W. DeLucia ◽  
Zeshan Ahmed ◽  
...  
Keyword(s):  
Single Dose ◽  
Mouse Model ◽  
Globoid Cell Leukodystrophy ◽  
Intracerebroventricular Administration ◽  
Globoid Cell

Mitigation of cerebellar neuropathy in globoid cell leukodystrophy mice by AAV-mediated gene therapy

Gene ◽  
2015 ◽  
Vol 571 (1) ◽  
pp. 81-90 ◽  
Author(s):  
Dar-Shong Lin ◽  
Chung-Der Hsiao ◽  
Allan Yueh-Luen Lee ◽  
Che-Sheng Ho ◽  
Hsuan-Liang Liu ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Globoid Cell Leukodystrophy ◽  
Globoid Cell

scholarly journals 888. Characterization of New Murine Models of Globoid Cell Leukodystrophy: Relevance for Gene Therapy Applications and Studies on Disease Pathogenesis

2006 ◽  
Vol 13 ◽  
pp. S342
Author(s):  
Ilaria Visigalli ◽  
Ubaldo del Carro ◽  
Letterio Politi ◽  
Angelo Quattrini ◽  
Paola Luzi ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Globoid Cell Leukodystrophy ◽  
Murine Models ◽  
Disease Pathogenesis ◽  
Globoid Cell
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