scholarly journals Neural Stem Cell Gene Therapy Ameliorates Pathology and Function in a Mouse Model of Globoid Cell Leukodystrophy

Stem Cells ◽  
2011 ◽  
Vol 29 (10) ◽  
pp. 1559-1571 ◽  
Author(s):  
Margherita Neri ◽  
Alessandra Ricca ◽  
Ilaria di Girolamo ◽  
Beatriz Alcala'-Franco ◽  
Chiara Cavazzin ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Stem Cell ◽  
Mouse Model ◽  
Neural Stem Cell ◽  
Globoid Cell Leukodystrophy ◽  
And Function ◽  
Cell Gene ◽  
Stem Cell Gene ◽  
Stem Cell Gene Therapy ◽  
Globoid Cell

scholarly journals Design of a regulated lentiviral vector for hematopoietic stem cell gene therapy of globoid cell leukodystrophy

2015 ◽  
Vol 2 ◽  
pp. 15038 ◽  
Author(s):  
Silvia Ungari ◽  
Annita Montepeloso ◽  
Francesco Morena ◽  
Fabienne Cocchiarella ◽  
Alessandra Recchia ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Stem Cell ◽  
Hematopoietic Stem Cell ◽  
Lentiviral Vector ◽  
Globoid Cell Leukodystrophy ◽  
Hematopoietic Stem ◽  
Cell Gene ◽  
Stem Cell Gene ◽  
Stem Cell Gene Therapy ◽  
Globoid Cell

scholarly journals Preclinical Efficacy and Safety Evaluation of Hematopoietic Stem Cell Gene Therapy in a Mouse Model of MNGIE

2018 ◽  
Vol 8 ◽  
pp. 152-165 ◽  
Author(s):  
Rana Yadak ◽  
Raquel Cabrera-Pérez ◽  
Javier Torres-Torronteras ◽  
Marianna Bugiani ◽  
Joost C. Haeck ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Stem Cell ◽  
Mouse Model ◽  
Safety Evaluation ◽  
Efficacy And Safety ◽  
Hematopoietic Stem ◽  
Preclinical Efficacy ◽  
Cell Gene ◽  
Stem Cell Gene ◽  
Stem Cell Gene Therapy

scholarly journals Unique anabolic action of stem cell gene therapy overexpressing PDGFB-DSS6 fusion protein in OVX osteoporosis mouse model

Bone Reports ◽  
2020 ◽  
Vol 12 ◽  
pp. 100236 ◽  
Author(s):  
Wanqiu Chen ◽  
Samiksha Wasnik ◽  
Yawen Fu ◽  
Leslie Aranda ◽  
Charles H. Rundle ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Stem Cell ◽  
Mouse Model ◽  
Fusion Protein ◽  
Anabolic Action ◽  
Cell Gene ◽  
Stem Cell Gene ◽  
Stem Cell Gene Therapy

Lentiviral mediated stem cell gene therapy corrects a mouse model of mucopolysaccharidosis type IIIA

2011 ◽  
Vol 102 (2) ◽  
pp. S8
Author(s):  
Brian Bigger ◽  
Alex Langford-Smith ◽  
Fiona Wilkinson ◽  
Kia Langford-Smith ◽  
Ana Sergijenko ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Stem Cell ◽  
Mouse Model ◽  
Mucopolysaccharidosis Type ◽  
Type Iiia ◽  
Cell Gene ◽  
Mucopolysaccharidosis Type Iiia ◽  
Stem Cell Gene ◽  
Stem Cell Gene Therapy

scholarly journals Lymphoid Development and Function in X-Linked Severe Combined Immunodeficiency Mice after Stem Cell Gene Therapy

2000 ◽  
Vol 1 (2) ◽  
pp. 145-153 ◽  
Author(s):  
Makoto Otsu ◽  
Stacie M. Anderson ◽  
David M. Bodine ◽  
Jennifer M. Puck ◽  
John J. O'Shea ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Stem Cell ◽  
Severe Combined Immunodeficiency ◽  
Combined Immunodeficiency ◽  
Lymphoid Development ◽  
And Function ◽  
Cell Gene ◽  
Stem Cell Gene ◽  
Stem Cell Gene Therapy

Regulatable Lentiviral Hematopoietic Stem Cell Gene Therapy in a Mouse Model of Parkinson's Disease

2018 ◽  
Vol 27 (14) ◽  
pp. 995-1005 ◽  
Author(s):  
Guo Ge ◽  
Cang Chen ◽  
Michael J. Guderyon ◽  
Jingwei Liu ◽  
Zhixu He ◽  
...  
Keyword(s):  
Parkinson’S Disease ◽  
Gene Therapy ◽  
Parkinson's Disease ◽  
Stem Cell ◽  
Mouse Model ◽  
Hematopoietic Stem Cell ◽  
Hematopoietic Stem ◽  
Cell Gene ◽  
Stem Cell Gene ◽  
Stem Cell Gene Therapy

Myeloid driven stem cell gene therapy corrects a mouse model of Mucopolysaccharidiosis IIIA

2013 ◽  
Vol 108 (2) ◽  
pp. S83
Author(s):  
Ana Sergijenko ◽  
Alexander Langford-Smith ◽  
Ai Yin Liao ◽  
Claire Pickford ◽  
John McDermott ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Stem Cell ◽  
Mouse Model ◽  
Cell Gene ◽  
Stem Cell Gene ◽  
Stem Cell Gene Therapy

Stem Cell Gene Therapy for Chronic Renal Failure

2003 ◽  
Vol 3 (5) ◽  
pp. 387-394 ◽  
Author(s):  
T. Yokoo ◽  
K. Sakurai ◽  
T. Ohashi ◽  
T. Kawamura
Keyword(s):  
Gene Therapy ◽  
Renal Failure ◽  
Stem Cell ◽  
Chronic Renal Failure ◽  
Cell Gene ◽  
Stem Cell Gene ◽  
Stem Cell Gene Therapy
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