scholarly journals Efficient AAV Vector Production System: Towards Gene Therapy For Duchenne Muscular Dystrophy

10.5772/53023 ◽  
2013 ◽  
Author(s):  
Takashi Okada
Keyword(s):  
Gene Therapy ◽  
Duchenne Muscular Dystrophy ◽  
Muscular Dystrophy ◽  
Production System ◽  
Aav Vector

scholarly journals Phase 1 Gene Therapy for Duchenne Muscular Dystrophy Using a Translational Optimized AAV Vector

2012 ◽  
Vol 20 (2) ◽  
pp. 443-455 ◽  
Author(s):  
Dawn E Bowles ◽  
Scott WJ McPhee ◽  
Chengwen Li ◽  
Steven J Gray ◽  
Jade J Samulski ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Duchenne Muscular Dystrophy ◽  
Muscular Dystrophy ◽  
Phase 1 ◽  
Aav Vector

scholarly journals Myostatin Is a Quantifiable Biomarker for Monitoring Pharmaco-gene Therapy in Duchenne Muscular Dystrophy

2020 ◽  
Vol 18 ◽  
pp. 415-421 ◽  
Author(s):  
Virginie Mariot ◽  
Caroline Le Guiner ◽  
Inès Barthélémy ◽  
Marie Montus ◽  
Stéphane Blot ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Duchenne Muscular Dystrophy ◽  
Muscular Dystrophy
Sign in / Sign up

Export Citation Format

Share Document