scholarly journals Neurodegeneration in spinal muscular atrophy: from disease phenotype and animal models to therapeutic strategies and beyond

2014 ◽  
Vol 9 (1) ◽  
pp. 49-65 ◽  
Author(s):  
Umrao R Monani ◽  
Darryl C De Vivo
Author(s):  
Sonia Messina ◽  
Maria Sframeli ◽  
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...  

2017 ◽  
pp. 221-239 ◽  
Author(s):  
P. O’Hern ◽  
E.L. Garcia ◽  
L.T. Hao ◽  
A.C. Hart ◽  
A.G. Matera ◽  
...  

2017 ◽  
Vol 26 (13) ◽  
pp. 2377-2385 ◽  
Author(s):  
Jeong-Ki Kim ◽  
Charlotte Caine ◽  
Tomoyuki Awano ◽  
Ruth Herbst ◽  
Umrao R. Monani

2017 ◽  
Vol 10 (8) ◽  
pp. 943-954 ◽  
Author(s):  
Melissa Bowerman ◽  
Catherina G. Becker ◽  
Rafael J. Yáñez-Muñoz ◽  
Ke Ning ◽  
Matthew J. A. Wood ◽  
...  

2012 ◽  
Vol 4 (13) ◽  
pp. 1733-1750 ◽  
Author(s):  
Jonathan J Cherry ◽  
Elliot J Androphy

2006 ◽  
Vol 7 (6) ◽  
pp. 381-386 ◽  
Author(s):  
Federica Sangiuolo ◽  
Annalisa Botta ◽  
Antonio Filareto ◽  
Paola Spitalieri ◽  
Giuseppe Novelli

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