scholarly journals Profile of alglucosidase alfa in the treatment of Pompe disease: safety, efficacy, and patient acceptability

2016 ◽  
pp. 1 ◽  
Author(s):  
Ilka Schneider ◽  
Stephan Zierz
Keyword(s):  
Pompe Disease ◽  
Patient Acceptability ◽  
Alglucosidase Alfa

Long-term efficacy of alglucosidase alfa in late-onset Pompe disease

2017 ◽  
Vol 120 (1-2) ◽  
pp. S134
Author(s):  
Ans van der Ploeg ◽  
Paula Clemens ◽  
Robert J Hopkin ◽  
Katherine Kacena ◽  
Bernd-Jan Sanson ◽  
...  
Keyword(s):  
Pompe Disease ◽  
Late Onset ◽  
Term Efficacy ◽  
Alglucosidase Alfa

A phase 4 prospective study in patients with adult Pompe disease treated with alglucosidase alfa

2015 ◽  
Vol 114 (2) ◽  
pp. S113-S114
Author(s):  
Beth L. Thurberg ◽  
Pierre Carlier ◽  
John T. Kissel ◽  
Benedikt Schoser ◽  
Alan Pestronk ◽  
...  
Keyword(s):  
Prospective Study ◽  
Pompe Disease ◽  
Alglucosidase Alfa

Alglucosidase alfa: first available treatment for Pompe disease

Therapy ◽  
2007 ◽  
Vol 4 (3) ◽  
pp. 271-277 ◽  
Author(s):  
Marc Nicolino
Keyword(s):  
Pompe Disease ◽  
Alglucosidase Alfa

scholarly journals Enzyme replacement therapy with alglucosidase alfa in Pompe disease: Clinical experience with rate escalation

2018 ◽  
Vol 123 (2) ◽  
pp. 92-96 ◽  
Author(s):  
Ankit K. Desai ◽  
Crista K. Walters ◽  
Heidi L. Cope ◽  
Zoheb B. Kazi ◽  
Stephanie M. DeArmey ◽  
...  
Keyword(s):  
Enzyme Replacement Therapy ◽  
Replacement Therapy ◽  
Clinical Experience ◽  
Pompe Disease ◽  
Enzyme Replacement ◽  
Alglucosidase Alfa

Higher dosing of alglucosidase alfa improves outcomes in children with Pompe disease

2020 ◽  
Vol 129 (2) ◽  
pp. S88
Author(s):  
Aleena A. Khan ◽  
Laura E. Case ◽  
Mrudu Herbert ◽  
Stephanie DeArmey ◽  
Harrison Jones ◽  
...  
Keyword(s):  
Pompe Disease ◽  
Alglucosidase Alfa
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