An open-label clinical trial of agalsidase alfa enzyme replacement therapy in children with Fabry disease who are naïve to enzyme replacement therapy

Drug Design Development and Therapy ◽

10.2147/dddt.s102761 ◽

2016 ◽

pp. 1771 ◽

Cited By ~ 9

Author(s):

Ozlem Goker-Alpan ◽

Nicola Longo ◽

Marie McDonald ◽

Suma Shankar ◽

Raphael Schiffmann ◽

...

Keyword(s):

Clinical Trial ◽

Enzyme Replacement Therapy ◽

Fabry Disease ◽

Replacement Therapy ◽

Open Label ◽

Enzyme Replacement ◽

Agalsidase Alfa

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An open-label, switchover trial to assess the safety and efficacy of agalsidase beta in patients with Fabry disease treated with agalsidase alfa enzyme replacement therapy

Molecular Genetics and Metabolism ◽

10.1016/j.ymgme.2013.12.217 ◽

2014 ◽

Vol 111 (2) ◽

pp. S90

Author(s):

Sarah Richards ◽

Dawn Laney ◽

Muhammad A. Pervaiz ◽

Suma Shankar

Keyword(s):

Enzyme Replacement Therapy ◽

Fabry Disease ◽

Replacement Therapy ◽

Agalsidase Beta ◽

Open Label ◽

Safety And Efficacy ◽

Enzyme Replacement ◽

Agalsidase Alfa

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Effects of enzyme replacement therapy on the cardiomyopathy of Anderson Fabry disease: a randomised, double-blind, placebo-controlled clinical trial of agalsidase alfa

Heart ◽

10.1136/hrt.2006.104026 ◽

2008 ◽

Vol 94 (2) ◽

pp. 153-158 ◽

Cited By ~ 196

Author(s):

D A Hughes ◽

P M Elliott ◽

J Shah ◽

J Zuckerman ◽

G Coghlan ◽

...

Keyword(s):

Clinical Trial ◽

Enzyme Replacement Therapy ◽

Fabry Disease ◽

Replacement Therapy ◽

Controlled Clinical Trial ◽

Double Blind ◽

Double Blind Placebo ◽

Enzyme Replacement ◽

Agalsidase Alfa

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Enzyme replacement therapy with agalsidase alfa in pregnant women with Fabry disease

European Journal of Obstetrics & Gynecology and Reproductive Biology ◽

10.1016/j.ejogrb.2009.01.007 ◽

2009 ◽

Vol 144 (1) ◽

pp. 92-93 ◽

Cited By ~ 21

Author(s):

G. Kalkum ◽

D. Macchiella ◽

J. Reinke ◽

H. Kölbl ◽

M. Beck

Keyword(s):

Enzyme Replacement Therapy ◽

Pregnant Women ◽

Fabry Disease ◽

Replacement Therapy ◽

Enzyme Replacement ◽

Agalsidase Alfa

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Successful Management of Enzyme Replacement Therapy in Related Fabry Disease Patients with Severe Adverse Events by Switching from Agalsidase Beta (Fabrazyme®) to Agalsidase Alfa (Replagal®)

10.1007/8904_2014_304 ◽

2014 ◽

Cited By ~ 1

Author(s):

Kazuya Tsuboi ◽

Hiroshi Yamamoto ◽

Fuji Somura ◽

Hiromi Goto

Keyword(s):

Adverse Events ◽

Enzyme Replacement Therapy ◽

Fabry Disease ◽

Replacement Therapy ◽

Agalsidase Beta ◽

Successful Management ◽

Enzyme Replacement ◽

Agalsidase Alfa ◽

Severe Adverse Events

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Safety and effectiveness of enzyme replacement therapy with agalsidase alfa in patients with Fabry disease: Post-marketing surveillance in Japan

Molecular Genetics and Metabolism ◽

10.1016/j.ymgme.2019.02.005 ◽

2019 ◽

Vol 126 (4) ◽

pp. 448-459 ◽

Cited By ~ 5

Author(s):

Hiroaki Sasa ◽

Munehiko Nagao ◽

Koichi Kino

Keyword(s):

Enzyme Replacement Therapy ◽

Fabry Disease ◽

Replacement Therapy ◽

Enzyme Replacement ◽

Agalsidase Alfa ◽

Post Marketing Surveillance ◽

Post Marketing

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Enzyme replacement therapy in Fabry disease: Comparison of agalsidase alfa and agalsidase beta

Molecular Genetics and Metabolism ◽

10.1016/j.ymgme.2008.07.002 ◽

2008 ◽

Vol 95 (1-2) ◽

pp. 114-115 ◽

Cited By ~ 15

Author(s):

Atul Mehta ◽

Michael Beck ◽

Christoph Kampmann ◽

Andrea Frustaci ◽

Dominique P. Germain ◽

...

Keyword(s):

Enzyme Replacement Therapy ◽

Fabry Disease ◽

Replacement Therapy ◽

Agalsidase Beta ◽

Enzyme Replacement ◽

Agalsidase Alfa

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Agalsidase alfa – a preparation for enzyme replacement therapy in Anderson–Fabry disease

Expert Opinion on Investigational Drugs ◽

10.1517/13543784.11.6.851 ◽

2002 ◽

Vol 11 (6) ◽

pp. 851-858 ◽

Cited By ~ 14

Author(s):

Michael Beck

Keyword(s):

Enzyme Replacement Therapy ◽

Fabry Disease ◽

Replacement Therapy ◽

Enzyme Replacement ◽

Agalsidase Alfa

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Efficacy and safety of enzyme-replacement-therapy with agalsidase alfa in 36 treatment-naïve Fabry disease patients

BMC Pharmacology and Toxicology ◽

10.1186/s40360-017-0152-7 ◽

2017 ◽

Vol 18 (1) ◽

Cited By ~ 5

Author(s):

Kazuya Tsuboi ◽

Hiroshi Yamamoto

Keyword(s):

Enzyme Replacement Therapy ◽

Fabry Disease ◽

Replacement Therapy ◽

Efficacy And Safety ◽

Enzyme Replacement ◽

Agalsidase Alfa ◽

Treatment Naïve

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Evaluation of Plasma Globotriaosylsphingosine in Patients with Anderson-Fabry Disease in Brazil on Enzyme Replacement Therapy with Agalsidase Alfa

Molecular Genetics and Metabolism ◽

10.1016/j.ymgme.2011.11.106 ◽

2012 ◽

Vol 105 (2) ◽

pp. S44

Author(s):

Charles Lourenco ◽

Janice Coelho ◽

Miguel Moyses Neto ◽

Osvaldo Merege Vieira Neto ◽

Wilson Marques

Keyword(s):

Enzyme Replacement Therapy ◽

Fabry Disease ◽

Replacement Therapy ◽

Enzyme Replacement ◽

Agalsidase Alfa

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Effects of enzyme replacement therapy with agalsidase alfa on glomerular filtration rate in patients with Fabry disease: preliminary data

Acta Paediatrica ◽

10.1111/j.1651-2227.2003.tb00214.x ◽

2007 ◽

Vol 92 ◽

pp. 14-15 ◽

Cited By ~ 7

Author(s):

F Dehout ◽

A Schwarting ◽

M Beck ◽

A Mehta ◽

R Ricci ◽

...

Keyword(s):

Glomerular Filtration Rate ◽

Enzyme Replacement Therapy ◽

Fabry Disease ◽

Replacement Therapy ◽

Glomerular Filtration ◽

Preliminary Data ◽

Filtration Rate ◽

Enzyme Replacement ◽

Agalsidase Alfa

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