Gene Therapy Using Hematopoietic Stem Cells

Gene Therapy With Modified Autologous Hematopoietic Stem Cells for Patients With Mucopolysaccharidosis Type IIIA

Case Medical Research ◽

10.31525/ct1-nct04201405 ◽

2019 ◽

Author(s):

Keyword(s):

Stem Cells ◽

Gene Therapy ◽

Hematopoietic Stem Cells ◽

Mucopolysaccharidosis Type ◽

Hematopoietic Stem ◽

Type Iiia ◽

Mucopolysaccharidosis Type Iiia

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Development of gene therapy for hematopoietic stem cells

Scandinavian Journal of Clinical and Laboratory Investigation ◽

10.1080/003655102320754700 ◽

2002 ◽

Vol 62 (5) ◽

pp. 10-10

Keyword(s):

Stem Cells ◽

Gene Therapy ◽

Hematopoietic Stem Cells ◽

Hematopoietic Stem

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Faculty Opinions recommendation of Successful gene therapy of Diamond-Blackfan anemia in a mouse model and human CD34+ cord blood hematopoietic stem cells using a clinically applicable lentiviral vector.

Faculty Opinions – Post-Publication Peer Review of the Biomedical Literature ◽

10.3410/f.739368425.793582178 ◽

2021 ◽

Author(s):

Frank Staal

Keyword(s):

Stem Cells ◽

Gene Therapy ◽

Mouse Model ◽

Hematopoietic Stem Cells ◽

Cord Blood ◽

Lentiviral Vector ◽

Hematopoietic Stem ◽

Diamond Blackfan Anemia ◽

Human Cd34

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Human Hematopoietic Stem Cells, Progenitors, and Peripheral Blood Lymphocytes as Targets for the Correction of Immune System Disorders via Gene Therapy

Molecular Biology of B-Cell and T-Cell Development ◽

10.1007/978-1-4757-2778-4_27 ◽

1998 ◽

pp. 545-571

Author(s):

Karen E. Pollok ◽

David A. Williams

Keyword(s):

Stem Cells ◽

Gene Therapy ◽

Immune System ◽

Hematopoietic Stem Cells ◽

Peripheral Blood ◽

Peripheral Blood Lymphocytes ◽

Hematopoietic Stem ◽

Blood Lymphocytes

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Experimental Approaches to Hemophilia Gene Therapy: Gene Transfer into Hematopoietic Stem Cells

33rd Hemophilia Symposium ◽

10.1007/978-3-642-18260-0_21 ◽

2004 ◽

pp. 153-158

Author(s):

A. Tiede ◽

M. Eder ◽

M. Scherr ◽

A. Ganser ◽

M. von Depka Prondzinski

Keyword(s):

Stem Cells ◽

Gene Therapy ◽

Gene Transfer ◽

Hematopoietic Stem Cells ◽

Hematopoietic Stem ◽

Experimental Approaches

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Genetically Modified Hematopoietic Stem Cells for Gene Therapy in Beta-Thalassemia: Power of Viral Vector Towards Clinical Application

10.2174/9789815036756121010011 ◽

2021 ◽

pp. 133-144

Keyword(s):

Stem Cells ◽

Gene Therapy ◽

Hematopoietic Stem Cells ◽

Clinical Application ◽

Viral Vector ◽

Genetically Modified ◽

Beta Thalassemia ◽

Hematopoietic Stem

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407. A Clinically-Relevant Gene Therapy Strategy for Hemophilia A: Non-Myeloablative Transplantation of Hematopoietic Stem Cells Transduced with a High-Expression Factor VIII Transgene

Molecular Therapy ◽

10.1016/s1525-0016(16)44613-7 ◽

2007 ◽

Vol 15 ◽

pp. S157

Keyword(s):

Stem Cells ◽

Gene Therapy ◽

Hematopoietic Stem Cells ◽

Factor Viii ◽

Hemophilia A ◽

High Expression ◽

Hematopoietic Stem ◽

Therapy Strategy ◽

Gene Therapy Strategy ◽

Relevant Gene

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Major Advances in the Development of Vectors for Clinical Gene Therapy of Hematopoietic Stem Cells from European Groups over the Last 25 Years

Human Gene Therapy ◽

10.1089/hum.2017.152 ◽

2017 ◽

Vol 28 (11) ◽

pp. 964-971 ◽

Cited By ~ 2

Author(s):

Anne Galy

Keyword(s):

Stem Cells ◽

Gene Therapy ◽

Hematopoietic Stem Cells ◽

Hematopoietic Stem ◽

Clinical Gene Therapy

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743. New Lentiviral Vectors for Gene Therapy of Thalassemia with the HPFH-2 Enhancer and the -117 HPFH Activating Mutation: Studies on Thalassemic Hematopoietic Stem Cells

Molecular Therapy ◽

10.1016/s1525-0016(16)40146-2 ◽

2008 ◽

Vol 16 ◽

pp. S278

Keyword(s):

Stem Cells ◽

Gene Therapy ◽

Hematopoietic Stem Cells ◽

Lentiviral Vectors ◽

Hematopoietic Stem ◽

Activating Mutation

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414. Mobilization of Hematopoietic Stem Cells with Plerixafor or Plerixafor+G-CSF for Human Gene Therapy of Thalassemia

Molecular Therapy ◽

10.1016/s1525-0016(16)36218-9 ◽

2012 ◽

Vol 20 ◽

pp. S161-S162

Keyword(s):

Stem Cells ◽

Gene Therapy ◽

Hematopoietic Stem Cells ◽

Human Gene ◽

Hematopoietic Stem ◽

Human Gene Therapy

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