scholarly journals Rationally Designed Base Editors for Precise Editing of the Sickle Cell Disease Mutation

2021 ◽  
Vol 4 (2) ◽  
pp. 169-177
Author(s):  
S. Haihua Chu ◽  
Michael Packer ◽  
Holly Rees ◽  
Dieter Lam ◽  
Yi Yu ◽  
...  
Keyword(s):  
Sickle Cell Disease ◽  
Sickle Cell ◽  
Cell Disease ◽  
Disease Mutation

scholarly journals 115. Correction of the Sickle-Cell Disease Mutation in Human Hematopoietic Stem/Progenitor Cells

2015 ◽  
Vol 23 ◽  
pp. S48
Author(s):  
Megan D. Hoban ◽  
Matthew C. Mendel ◽  
Zulema Romero ◽  
Michael L. Kaufman ◽  
Alok V. Joglekar ◽  
...  
Keyword(s):  
Sickle Cell Disease ◽  
Progenitor Cells ◽  
Sickle Cell ◽  
Cell Disease ◽  
Hematopoietic Stem ◽  
Disease Mutation

scholarly journals 338. Evaluation of TALENs and the CRISPR/Cas9 Nuclease System To Correct the Sickle Cell Disease Mutation

2015 ◽  
Vol 23 ◽  
pp. S135
Author(s):  
Megan D. Hoban ◽  
Dianne Lumaquin ◽  
Caroline Kuo ◽  
Zulema Romero ◽  
Courtney Young ◽  
...  
Keyword(s):  
Sickle Cell Disease ◽  
Sickle Cell ◽  
Cell Disease ◽  
Disease Mutation ◽  
Cas9 Nuclease

Somatic mosaicism for chromosome X and Y aneuploidies in monozygotic twins heterozygous for sickle cell disease mutation

2010 ◽  
Vol 152A (10) ◽  
pp. 2595-2598 ◽  
Author(s):  
Hamid Reza Razzaghian ◽  
Mehdi Hayat Shahi ◽  
Lars A. Forsberg ◽  
Teresita Diaz de Ståhl ◽  
Devin Absher ◽  
...  
Keyword(s):  
Sickle Cell Disease ◽  
Sickle Cell ◽  
Somatic Mosaicism ◽  
Monozygotic Twins ◽  
Cell Disease ◽  
Chromosome X ◽  
Disease Mutation

scholarly journals Editing the Sickle Cell Disease Mutation in Human Hematopoietic Stem Cells: Comparison of Endonucleases and Homologous Donor Templates

2019 ◽  
Vol 27 (8) ◽  
pp. 1389-1406 ◽  
Author(s):  
Zulema Romero ◽  
Anastasia Lomova ◽  
Suzanne Said ◽  
Alexandra Miggelbrink ◽  
Caroline Y. Kuo ◽  
...  
Keyword(s):  
Stem Cells ◽  
Sickle Cell Disease ◽  
Hematopoietic Stem Cells ◽  
Sickle Cell ◽  
Cell Disease ◽  
Hematopoietic Stem ◽  
Disease Mutation
Sign in / Sign up

Export Citation Format

Share Document