Phase I Trial of Intranasal and Endobronchial Administration of a Recombinant Adeno-Associated Virus Serotype 2 (rAAV2)-CFTR Vector in Adult Cystic Fibrosis Patients: A Two-Part Clinical Study

2003 ◽  
Vol 14 (11) ◽  
pp. 1079-1088 ◽  
Author(s):  
Terence R. Flotte ◽  
Pamela L. Zeitlin ◽  
Thomas C. Reynolds ◽  
Alison E. Heald ◽  
Patty Pedersen ◽  
...  
Keyword(s):  
Cystic Fibrosis ◽  
Clinical Study ◽  
Phase I ◽  
Phase I Trial ◽  
Adeno Associated Virus ◽  
Virus Serotype ◽  
Endobronchial Administration

Phase I Trial of Intramuscular Injection of a Recombinant Adeno-associated Virus Serotype 2 ?1-Antitrypsin (AAT) Vector in AAT-Deficient Adults

2006 ◽  
Vol 0 (0) ◽  
pp. 061121084323001
Author(s):  
Mark L. Brantly ◽  
L. Terry Spencer ◽  
Margaret Humphries ◽  
Thomas J. Conlon ◽  
Carolyn T. Spencer ◽  
...  
Keyword(s):  
Phase I ◽  
Intramuscular Injection ◽  
Phase I Trial ◽  
Adeno Associated Virus ◽  
Virus Serotype

Phase I Trial of Intramuscular Injection of a Recombinant Adeno-Associated Virus Serotype 2α1-Antitrypsin (AAT) Vector in AAT-Deficient Adults

2006 ◽  
Vol 17 (12) ◽  
pp. 1177-1186 ◽  
Author(s):  
Mark L. Brantly ◽  
L. Terry Spencer ◽  
Margaret Humphries ◽  
Thomas J. Conlon ◽  
Carolyn T. Spencer ◽  
...  
Keyword(s):  
Phase I ◽  
Intramuscular Injection ◽  
Phase I Trial ◽  
Adeno Associated Virus ◽  
Virus Serotype

Phase I Trial of Intramuscular Injection of a Recombinant Adeno-Associated Virus Serotype 2?1-Antitrypsin (AAT) Vector in AAT-Deficient Adults

2006 ◽  
Vol 0 (0) ◽  
pp. 061211062938001
Author(s):  
Mark L. Brantly ◽  
L. Terry Spencer ◽  
Margaret Humphries ◽  
Thomas J. Conlon ◽  
Carolyn T. Spencer ◽  
...  
Keyword(s):  
Phase I ◽  
Intramuscular Injection ◽  
Phase I Trial ◽  
Adeno Associated Virus ◽  
Virus Serotype

scholarly journals A phase I trial of adeno-associated virus serotype 1-γ-sarcoglycan gene therapy for limb girdle muscular dystrophy type 2C

Brain ◽  
2011 ◽  
Vol 135 (2) ◽  
pp. 483-492 ◽  
Author(s):  
Serge Herson ◽  
Faycal Hentati ◽  
Aude Rigolet ◽  
Anthony Behin ◽  
Norma B. Romero ◽  
...  
Keyword(s):  
Gene Therapy ◽  
Muscular Dystrophy ◽  
Phase I ◽  
Phase I Trial ◽  
Limb Girdle Muscular Dystrophy ◽  
Adeno Associated Virus ◽  
Virus Serotype ◽  
Serotype 1

Gene Therapy for Cystic Fibrosis Using E1-Deleted Adenovirus: A Phase I Trial in the Nasal Cavity. University of North Carolina at Chapel Hill, Chapel Hill, North Carolina

1994 ◽  
Vol 5 (5) ◽  
pp. 615-639 ◽  
Author(s):  
Richard C. Boucher ◽  
Michael R. Knowles ◽  
Larry G. Johnson ◽  
John C. Olsen ◽  
Raymond Pickles ◽  
...  
Keyword(s):  
Cystic Fibrosis ◽  
Gene Therapy ◽  
North Carolina ◽  
Phase I ◽  
Nasal Cavity ◽  
Phase I Trial ◽  
University Of North Carolina ◽  
Chapel Hill

Phase I Trial of Leber Congenital Amaurosis due to RPE65 Mutations by Ocular Subretinal Injection of Adeno-Associated Virus Gene Vector: Short-Term Results

2008 ◽  
Vol 0 (ja) ◽  
pp. 081015093227032 ◽  
Author(s):  
William Hauswirth ◽  
Tomas S Aleman ◽  
Shalesh Kaushal ◽  
Artur V Cideciyan ◽  
Sharon B Schwartz ◽  
...  
Keyword(s):  
Phase I ◽  
Phase I Trial ◽  
Gene Vector ◽  
Short Term ◽  
Adeno Associated Virus ◽  
Leber Congenital Amaurosis ◽  
Virus Gene ◽  
Subretinal Injection

A Phase I Trial of Intranasal Moli1901 for Cystic Fibrosis

CHEST Journal ◽  
2004 ◽  
Vol 125 (1) ◽  
pp. 143-149 ◽  
Author(s):  
Pamela L. Zeitlin ◽  
Michael P. Boyle ◽  
William B. Guggino ◽  
Luis Molina
Keyword(s):  
Cystic Fibrosis ◽  
Phase I ◽  
Phase I Trial

Safety and tolerability of gene therapy with an adeno-associated virus (AAV) borne GAD gene for Parkinson's disease: an open label, phase I trial

The Lancet ◽  
2007 ◽  
Vol 369 (9579) ◽  
pp. 2097-2105 ◽  
Author(s):  
Michael G Kaplitt ◽  
Andrew Feigin ◽  
Chengke Tang ◽  
Helen L Fitzsimons ◽  
Paul Mattis ◽  
...  
Keyword(s):  
Parkinson’S Disease ◽  
Gene Therapy ◽  
Parkinson's Disease ◽  
Phase I ◽  
Phase I Trial ◽  
Open Label ◽  
Adeno Associated Virus ◽  
Open Label Phase
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