scholarly journals Enzyme replacement in the CSF to treat metachromatic leukodystrophy in mouse model using single intracerebroventricular injection of self-complementary AAV1 vector

2015 ◽  
Vol 5 (1) ◽  
Author(s):  
Kohei Hironaka ◽  
Yoshiyuki Yamazaki ◽  
Yukihiko Hirai ◽  
Motoko Yamamoto ◽  
Noriko Miyake ◽  
...  
2005 ◽  
Vol 14 (9) ◽  
pp. 1139-1152 ◽  
Author(s):  
Ulrich Matzner ◽  
Eva Herbst ◽  
Kerstin Khalaj Hedayati ◽  
Renate Lüllmann-Rauch ◽  
Carsten Wessig ◽  
...  

2009 ◽  
Vol 17 (4) ◽  
pp. 600-606 ◽  
Author(s):  
Ulrich Matzner ◽  
Renate Lüllmann-Rauch ◽  
Stijn Stroobants ◽  
Claes Andersson ◽  
Cecilia Weigelt ◽  
...  

2012 ◽  
Vol 21 (11) ◽  
pp. 2599-2609 ◽  
Author(s):  
F. Matthes ◽  
S. Stroobants ◽  
D. Gerlach ◽  
C. Wohlenberg ◽  
C. Wessig ◽  
...  

2007 ◽  
Vol 15 (1) ◽  
pp. 38-43 ◽  
Author(s):  
Toshiyuki Kurai ◽  
Sanae Hisayasu ◽  
Ryo Kitagawa ◽  
Makoto Migita ◽  
Hidenori Suzuki ◽  
...  

2000 ◽  
Vol 14 (2) ◽  
pp. 361-367 ◽  
Author(s):  
Ulla Dunder ◽  
Vesa Kaartinen ◽  
Pirjo Valtonen ◽  
Eira VÄÄnÄnen ◽  
Veli-Matti Kosma ◽  
...  

1976 ◽  
Vol 35 (6) ◽  
pp. 622-632 ◽  
Author(s):  
S. E. Poduslo ◽  
G. Tennekoon ◽  
D. Price ◽  
K. Miller ◽  
G. M. McKhann

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