Correction of Glycogen Storage Disease Type II by Enzyme Replacement with a Recombinant Human Acid Maltase Produced by Over-Expression in a CHO-DHFRneg Cell Line

2000 ◽  
Vol 276 (3) ◽  
pp. 917-923 ◽  
Author(s):  
Frank Martiniuk ◽  
Agnes Chen ◽  
Vincent Donnabella ◽  
Eleni Arvanitopoulos ◽  
Alfred E. Slonim ◽  
...  
Keyword(s):  
Cell Line ◽  
Storage Disease ◽  
Glycogen Storage Disease Type ◽  
Glycogen Storage ◽  
Disease Type ◽  
Type Ii ◽  
Over Expression ◽  
Enzyme Replacement ◽  
Acid Maltase ◽  
Human Acid

Recombinant human acid ??-glucosidase enzyme therapy for infantile glycogen storage disease type II: Results of a phase I/II clinical trial

2001 ◽  
Vol 3 (2) ◽  
pp. 132-138 ◽  
Author(s):  
Andrea Amalfitano ◽  
A. Resai Bengur ◽  
Richard P. Morse ◽  
Joseph M. Majure ◽  
Laura E. Case ◽  
...  
Keyword(s):  
Clinical Trial ◽  
Phase I ◽  
Glycogen Storage Disease ◽  
Storage Disease ◽  
Glycogen Storage Disease Type ◽  
Glycogen Storage ◽  
Disease Type ◽  
Type Ii ◽  
Enzyme Therapy ◽  
Human Acid

scholarly journals Recombinant human acid α-glucosidase enzyme therapy for infantile glycogen storage disease type II: Results of a phase I/II clinical trial

2001 ◽  
Vol 3 (2) ◽  
pp. 132-138
Author(s):  
Andrea Amalfitano ◽  
A. Resai Bengur ◽  
Richard P. Morse ◽  
Joseph M. Majure ◽  
Laura E. Case ◽  
...  
Keyword(s):  
Clinical Trial ◽  
Phase I ◽  
Glycogen Storage Disease ◽  
Storage Disease ◽  
Glycogen Storage Disease Type ◽  
Glycogen Storage ◽  
Disease Type ◽  
Type Ii ◽  
Enzyme Therapy ◽  
Human Acid

scholarly journals Human Acid  -Glucosidase from Rabbit Milk Has Therapeutic Effect in Mice with Glycogen Storage Disease Type II

1999 ◽  
Vol 8 (12) ◽  
pp. 2145-2153 ◽  
Author(s):  
A. G. A. Bijvoet ◽  
H. Van Hirtum ◽  
M. A. Kroos ◽  
E. H. M. Van de Kamp ◽  
O. Schoneveld ◽  
...  
Keyword(s):  
Therapeutic Effect ◽  
Glycogen Storage Disease ◽  
Storage Disease ◽  
Glycogen Storage Disease Type ◽  
Glycogen Storage ◽  
Disease Type ◽  
Type Ii ◽  
Human Acid ◽  
Rabbit Milk

Effects of enzyme replacement therapy on five patients with advanced late-onset glycogen storage disease type II: a 2-year follow-up study

2011 ◽  
Vol 35 (2) ◽  
pp. 301-310 ◽  
Author(s):  
Yoshihiko Furusawa ◽  
Madoka Mori-Yoshimura ◽  
Toshiyuki Yamamoto ◽  
Chikako Sakamoto ◽  
Mizuki Wakita ◽  
...  
Keyword(s):  
Enzyme Replacement Therapy ◽  
Storage Disease ◽  
Late Onset ◽  
Glycogen Storage Disease Type ◽  
Glycogen Storage ◽  
Disease Type ◽  
Type Ii ◽  
Enzyme Replacement ◽  
Follow Up Study
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