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TSNP : A two‐stage nonparametric phase I/ II clinical trial design for immunotherapy
Pharmaceutical Statistics
◽
10.1002/pst.2075
◽
2020
◽
Author(s):
Yan Han
◽
Hao Liu
◽
Sha Cao
◽
Chi Zhang
◽
Yong Zang
Keyword(s):
Clinical Trial
◽
Phase I
◽
Trial Design
◽
Clinical Trial Design
◽
Two Stage
Download Full-text
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Two-stage model-based clinical trial design to optimize phase I development of novel anticancer agents
Investigational New Drugs
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10.1007/s10637-008-9216-2
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2009
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Vol 28
(1)
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pp. 61-75
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Author(s):
Anthe S. Zandvliet
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Mats O. Karlsson
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...
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Stage Model
◽
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Phase I/II clinical trial design for a novel therapy for mucopolysaccharidosis type I with an intravenously administered blood-brain barrier-crossing enzyme (JR-171)
Molecular Genetics and Metabolism
◽
10.1016/j.ymgme.2020.12.105
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2021
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Keyword(s):
Clinical Trial
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Phase I
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Blood Brain Barrier
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Trial Design
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Clinical Trial Design
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Brain Barrier
◽
Type I
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Mucopolysaccharidosis Type
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Mucopolysaccharidosis Type I
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Novel Therapy
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Extending the two‐stage single arm phase II clinical trial design to the delayed response scenario
Pharmaceutical Statistics
◽
10.1002/pst.2171
◽
2021
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Author(s):
Bo Chen
◽
Xing Zhao
◽
Juying Zhang
Keyword(s):
Clinical Trial
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Phase Ii
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Trial Design
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Clinical Trial Design
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Phase Ii Clinical Trial
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Is the “3+3” Dose-Escalation Phase I Clinical Trial Design Suitable for Therapeutic Cancer Vaccine Development? A Recommendation for Alternative Design
Clinical Cancer Research
◽
10.1158/1078-0432.ccr-13-2671
◽
2014
◽
Vol 20
(18)
◽
pp. 4758-4767
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Author(s):
Osama E. Rahma
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Keyword(s):
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Phase I
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Early 3+3 Trial Dose-Escalation Phase I Clinical Trial Design and Suitability for Immune Checkpoint Inhibitors
Clinical Cancer Research
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10.1158/1078-0432.ccr-20-2669
◽
2020
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Author(s):
Osama E. Rahma
◽
Joshua E. Reuss
◽
Anita Giobbie-Hurder
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Ghazaleh Shoja E Razavi
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...
Keyword(s):
Clinical Trial
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Phase I
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Dose Escalation
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Immune Checkpoint
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Trial Design
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Immune Checkpoint Inhibitors
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Checkpoint Inhibitors
◽
Clinical Trial Design
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Phase I Clinical Trial
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Adaptive Phase I clinical trial design using Markov models for conditional probability of toxicity
Journal of Biopharmaceutical Statistics
◽
10.1080/10543406.2015.1052492
◽
2015
◽
Vol 26
(3)
◽
pp. 475-498
◽
Cited By ~ 4
Author(s):
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◽
Jeremy M. G. Taylor
◽
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Keyword(s):
Clinical Trial
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Phase I
◽
Conditional Probability
◽
Trial Design
◽
Markov Models
◽
Clinical Trial Design
◽
Phase I Clinical Trial
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A two‐stage phase II clinical trial design with nested criteria for early stopping and efficacy
Pharmaceutical Statistics
◽
10.1002/pst.1965
◽
2019
◽
Vol 18
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◽
pp. 700-713
Author(s):
Michelle DeVeaux
◽
Michael Kane
◽
Wei Wei
◽
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Keyword(s):
Clinical Trial
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Phase Ii
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Trial Design
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Clinical Trial Design
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Phase Ii Clinical Trial
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Early Stopping
◽
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Operating characteristics of a Simon two-stage phase II clinical trial design incorporating continuous toxicity monitoring
Pharmaceutical Statistics
◽
10.1002/pst.510
◽
2012
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Vol 11
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pp. 170-176
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Cited By ~ 4
Author(s):
H.E. Ray
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The benefits of including expansion cohorts in Phase I oncology clinical trial design
Clinical Investigation
◽
10.4155/cli.14.40
◽
2014
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Vol 4
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pp. 481-482
Author(s):
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Albiruni RA Razak
Keyword(s):
Clinical Trial
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Phase I
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Trial Design
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Clinical Trial Design
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Oncology Clinical Trial
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A Bayesian-frequentist two-stage single-arm phase II clinical trial design
Statistics in Medicine
◽
10.1002/sim.5330
◽
2012
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Vol 31
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pp. 2055-2067
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Cited By ~ 14
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Keyword(s):
Clinical Trial
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Phase Ii
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Trial Design
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Clinical Trial Design
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Phase Ii Clinical Trial
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Two Stage
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