Correction of mucopolysaccharidosis type IIIA somatic and central nervous system pathology by lentiviral-mediated gene transfer

2010 ◽  
Vol 12 (9) ◽  
pp. 717-728 ◽  
Author(s):  
Chantelle McIntyre ◽  
Sharon Byers ◽  
Donald S. Anson
2017 ◽  
Vol 28 (8) ◽  
pp. 626-638 ◽  
Author(s):  
Kanut Laoharawee ◽  
Kelly M. Podetz-Pedersen ◽  
Tam T. Nguyen ◽  
Laura B. Evenstar ◽  
Kelley F. Kitto ◽  
...  

2010 ◽  
Vol 100 (2) ◽  
pp. 168-175 ◽  
Author(s):  
Adeline A. Lau ◽  
John J. Hopwood ◽  
Eric J. Kremer ◽  
Kim M. Hemsley

2014 ◽  
Vol 1 ◽  
pp. 422-424 ◽  
Author(s):  
Erlane Marques Ribeiro ◽  
Ana Carolina Brusius-Facchin ◽  
Sandra Leistner-Segal ◽  
Carlos Antônio Bruno da Silva ◽  
Ida Vanessa Schwartz

2013 ◽  
Vol 40 (9) ◽  
pp. 1420-1427 ◽  
Author(s):  
Scarlett Lewitschnig ◽  
Keerti Gedela ◽  
Martina Toby ◽  
Ranjababu Kulasegaram ◽  
Mark Nelson ◽  
...  

Sign in / Sign up

Export Citation Format

Share Document